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Spotlight on Gene Therapy: finding a Cure

Awards for Mueller Lab at ASGCT 2017

Posted On: Saturday, May 13, 2017 Posted By: Florie Borel Tags: Alpha-one antitrypsin, Amyotrophic lateral sclerosis, Gene Therapy, Presentations

We are thrilled that our lab received several distinctions during ASGCT 2017!


Three of the five abstracts we submitted were selected as Top Abstracts:

Proof-of-Concept for Non-Nuclease-Mediated Genome Editing to Treat Alpha-1 Antitrypsin Deficiency, presented by Florie Borel

Artificial miRNAs Reduce Human Huntingtin Throughout the Striatum in a Transgenic Sheep Model of Huntington’s Disease, presented by Edith Pfister

Silencing SOD1 to Treat Amyotrophic Lateral Sclerosis: Preclinical Studies in Cynomolgus Monkeys, presented by Florie Borel

In addition, Florie Borel received a Travel Award to attend ASGCT.


Thank you to ASGCT for recognizing our work! We are looking forward to next year's conference in Chicago!