Welcome to the Flotte Lab for Gene Therapy
Our Lab
Gene therapy treatment for genetic diseases that affect children
Our lab is currently investigating the use of gene therapy for genetic diseases that affect children, including cystic fibrosis, alpha-1 antitrypsin (AAT) deficiency, type I diabetes, and disorders of fatty acid oxidation. We are studying adeno-associated virus (AAV) vectors and the mechanisms of AAV persistence, since these represent the basis for a more profound understanding of the potential for long-term safe and effective gene therapy. We are currently conducting Phase I trials with rAAV expressing alpha-1antitrypsin in AAT-deficient patients.
Partner with Us
Partnership opportunities
Our lab is always interested in possible partnerships with both indivituals and organizations. Some possible partnerships include knowledge exchange, consulting, collaborations with academia and/or industry, sponsored research, spinout activities and reagent exchange. Read more
We believe that great scientific discoveries happen when people work together.
Let's have the next big breakthrough together!
Explore our Research Partnership Opportunities